An estimated 15-20 per cent of children diagnosed with Dravets Syndrome die before reaching adulthood. There is no cure, and current treatment focuses on simply reducing seizures.
The trial, led by consultant neurologist Dr Catherine Mummery (UCL Queen Square Institute of Neurology & the National Hospital for Neurology and Neurosurgery), represents the first time that a 'gene silencing' approach has been taken in dementia and Alzheimer's disease.