New York [US], December 27 (ANI): According to a study, a single dose restored blood cells to their normal shape and eliminated the most serious complication of sickle cell disease for at least three years in some patients.
Washington [US], October 9 (ANI): A research team led by Purdue University's Alexander Chubykin, an associate professor of biological sciences in the College of Science, in collaboration with the team led by Gong Chen at Jinan University, China, has discovered a way to use gene therapy to tu
Ohio [US], July 12 (ANI): Researchers recently developed a novel method of gene therapy that can help children born with a rare genetic disorder called AADC deficiency. This deficiency causes severe physical and developmental disabilities.
California [US], May 11 (ANI): Researchers have developed a gene therapy that successfully treated 48 out of 50 children with a form of severe combined immunodeficiency that leaves them without an immune system.
Philadelphia (Pennsylvania) [US], May 2 (ANI): A recent study's initial data from a clinical trial led by researchers found that new gene therapy for one of the most common forms of congenital blindness was safe and improved patients' vision.
Philadelphia (Pennsylvania) [US], April 25 (ANI): According to initial data from a clinical trial led by researchers, new gene therapy for one of the most common forms of congenital blindness was safe and improved patients' vision.
Philadelphia (Pennsylvania) [US], April 20 (ANI): A new gene therapy for one of the most common forms of congenital blindness was safe and improved patients' vision, according to initial data from a clinical trial led by researchers.
Boston [US], March 20 (ANI): Researchers have used a genetic engineering strategy to dramatically reduce levels of tau--a key protein that accumulates and becomes tangled in the brain during the development of Alzheimer's disease--in an animal model of the condition.
Washington [US], March 17 (ANI): During an international collaboration recently between Great Ormond Street Hospital, the UCL GOS Institute for Child Health, and Harvard Medical School, it was found that the beneficial effects of gene therapy can be seen decades after the transplanted blood
Washington [US], January 31 (ANI): Researchers at Children's Hospital of Philadelphia (CHOP) have developed a potentially safer and more effective gene therapy vector for blood disorders.
New York [US], January 20 (ANI): A study published in journal Human Gene Therapy shows that gene editing therapies, including CRISPR-Cas frameworks, offer the possibility to address transformations causing inherited retinal degenerations, a leading cause of blindness.